Module Leader Professor Alan Mackay-Sim
 Host Organisation National Centre for Adult Stem Cell Research, Griffith University

Module description

Most brain disorders and diseases arise from complex interactions between multiple genes and multiple environmental risk factors. Stem cells may provide useful cellular models to dissect out the cellular and molecular causes of brain diseases but up to now, iPS cells have been derived mostly from persons with diseases caused by single gene mutations that have large cellular effects with less influence of environmental risk factors. In comparison, the cellular effects of complex diseases may be much more subtle, depending on the interplay of many genes acting in gene networks and metabolic pathways.

This module investigates iPS cells generated from skin fibroblasts from people with schizophrenia, a complex brain disease with strong genetic and environmental risks but no known gene mutations. Previous experiments demonstrate that skin fibroblasts from patients with schizophrenia do not demonstrate disease related differences in gene expression. The first question is whether iPS reprogramming of these skin fibroblasts will reveal disease related information which was not present beforehand. The second question is whether differentiating the iPS cells into neurons is required to reveal disease related information. iPS cell lines from multiple patients and controls will be compared for their gene expression to investigate variability due to individual donor and disease status.

Module Leader biography

Professor Alan Mackay-Sim is Director of the National Centre for Adult Stem Cell Research. The Centre investigates adult stem cells from the organ of smell in the nose, which regenerates its sensory neurons throughout life. Professor Mackay-Sim was scientific director of a clinical trial where olfactory ensheathing cells were taken from the nose of people with paraplegia and transplanted into their own injured spinal cord. This trial provides a precedent for future trials using adult stem cells.

Professor Mackay-Sim and his team identified a stem cell in olfactory mucosa that is pluripotent, capable of making all cells of the body. They showed these cells were therapeutic when transplanted into the brain of the rat model of Parkinson’s disease. They are using olfactory stem cells as cellular models of brain diseases and have demonstrated key alterations in gene and protein expression and cell function in schizophrenia and Parkinson’s disease.

Contact details

 E-mail  a.mackay-sim@griffith.edu.au
 Phone   +61 7 3735 4233

Selected publications

  1. Mackay-Sim A, Kittel P (1991) Cell dynamics in the adult mouse olfactory epithelium: a quantitative autoradiographic study. Journal of Neuroscience. 11:979-984.
  2. Mackay-Sim A, Kittel P (1991) On the life span of olfactory receptor neurones. European Journal of Neuroscience. 3:209-215.
  3. Féron F, Perry C, McGrath JJ, Mackay-Sim A (1998) New techniques for biopsy and culture of human olfactory epithelial neurons. Archives of Otolaryngology Head and Neck Surgery 124:861-866.
  4. Newman M, Féron F and Mackay-Sim A (2000) Growth factor control of olfactory neurogenesis. Neuroscience 99:343-350.
  5. Newman M, Féron F and Mackay-Sim A (2000) Growth factor regulation of neurogenesis in adult olfactory epithelium. Neuroscience 99:343-350.
  6. Lu J, Féron F, Ho SM, Mackay-Sim A and Waite PME (2001) Transplantation of nasal olfactory tissue promotes partial recovery in paraplegic adult rats. Brain Research 889:344-357.
  7. Lu J, Féron F, Mackay-Sim A and Waite PME (2002) Olfactory ensheathing cells promote locomotor recovery after delayed transplantation into transected spinal cord. Brain 125: 14-21.
  8. Murrell W, Wetzig A, Donnellan M, Féron F, Burne TH, Meedeniya ACB, Kesby J, Bianco J, Perry C, Silburn PA, Mackay-Sim A (2008) Olfactory mucosa is potential source for autologous stem cell therapy for Parkinson's disease. Stem Cells 26:2183-2192.
  9. Féron F, Perry C, Cochrane J, Licina P, Nowitzke A, Uquhart S, Geraghty T, Mackay-Sim A (2005) Autologous olfactory ensheathing cell transplantation in human spinal cord injury. Brain 128:2951-2960.
  10. Mackay-Sim A, Féron F, Cochrane J, Bassingthwaighte L, Bayliss C, Davies, W, Fronek P, Gray C, Kerr G, Licina P, Nowitzke A, Perry C, Silburn PAS, Urquhart S and Geraghty T  (2008) Autologous olfactory ensheathing cell transplantation in human paraplegia: a 3 year clinical trial. Brain 131:2376-2386